Research Awardees

Current CFRI-Funded Cystic Fibrosis Researchers

2025 – 2027

Elizabeth Nash Memorial Fellowship Program

 

Paul Bollyky, MD, PhD

Paul Bollyky, MD, PhD, Principal Investigator
Samuel Rodriguez-Perez, PhD, MS, Postdoctoral Fellow
Stanford University
Development of a Phage-Based Gene Delivery Platform for Restoring Wild-Type CFTR Expression in the Human Lung Epithelia

Sriram Vaidyanathan, PhD, Principal Investigator
Brodie Ranzau, PhD, Postdoctoral Fellow
The Research Institute at Nationwide Children’s Hospital
Gene Insertion of a Gain of Function Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Variant to Improve CFTR-Mediated Ion Transport

 

Katrine Whiteson, PhD, Principal Investigator
Sage Dunham, PhD, Postdoctoral Fellow
University of California Irvine
Overcoming Evolved Bacteriophage Resistance Via Next-Generation Directed Evolution

 

New Horizons Program

 

Ashley Cooney, PhD, Principal Investigator
University of Iowa
Permanent Gene Repair by AAV-mediated Base Editing in CF Pigs

 

Ruobing Wang, MD, Principal Investigator
Boston Children’s Hospital
Studying Pulmonary Ionocyte Differentiation and Function Using Stem Cell Derived Airways

 

Daniel Wolter, PhD, Principal Investigator
University of Washington
Role of Bacterial Metabolism in Promoting Antibiotic-Tolerant Staphylococcus Aureus CF Infections

 

2024 – 2026

Elizabeth Nash Memorial Fellowship Program

 

Steven Jonas, MD, PhD, Principal Investigator
Ruby Sims, PhD, Postdoctoral Fellow
University of California Los Angeles
Designing a cystic fibrosis gene therapy nanocarrier platform to target and modify airway stem cell-derived ionocytes

Ron Kopito, PhD, Principal Investigator
Celeste Riepe, PhD, Postdoctoral Fellow
Stanford University
Pharmacogenomic discovery of therapeutic targets for corrector-resistant cystic fibrosis

 

New Horizons Program

 

Daria Van Tyne, PhD, Principal Investigator
University of Pittsburgh
Optimization of activity and improved delivery of bacteriophages targeting Burkholderia spp

 

 

Feng Yuan, PhD, Principal Investigator
University of Alabama at Birmingham
Dissecting Pulmonary ionocyte subtypes and their functional roles in cystic fibrosis

 

2023 – 2025

Elizabeth Nash Memorial Fellowship Program

 

Matthew Porteus, MD, PhD, Principal Investigator
Anais Amaya Colina, PhD, Postdoctoral Fellow
Stanford University
A Hybrid Gene Correction Strategy for Cystic Fibrosis

 

New Horizons Program

 

Nadia Ameen, MD, Principal Investigator
Yale University School of Medicine
Elucidating the ion transport functions of CFTR High Expresser Cells (CHEs) and its relevance to intestinal disease in Cystic Fibrosis (CF)

 

 

Benjamin Chan, PhD, Principal Investigator
Yale University School of Medicine
Optimization of Phage Therapy to Reduce Pseudomonas-Induced Inflammation in Cystic Fibrosis

 

 

Katrine Whiteson, PhD, Principal Investigator
University of California Irvine
Targeting recalcitrant CF pathogens with phages, antibiotics, and small molecule adjuvants